Regulatory Norgine gets first EU approval for WHIM syndrome therapy PharmaphorumPatients in the EU with the ultra-rare disease WHIM syndrome now have their first approved treatment, Norgine's Xolremdi.Rare DiseaseRead full story pharminent April 30, 2026 (Last updated: April 30, 2026) Pharmaphorum Patients in the EU with the ultra-rare disease WHIM syndrome now have their first approved treatment, Norgine’s Xolremdi. Rare Disease Read full story Post navigation Previous: Regeneron Q1 2026 net income falls 10% to $727mNext: GSK-partnered Alector hit with third neuro failure as Alzheimer’s asset disappoints Related Stories Regulatory Ultragenyx wins FDA approval for first treatment targeting root cause of GSDIa pharminent August 20, 2026 Regulatory Regeneron wins FDA approval to challenge Ipsen for rare bone disease market pharminent August 20, 2026 Regulatory FDA grants accelerated approval to Ultragenyx’s Genglycos gene therapy pharminent August 20, 2026
